Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after over 300 days at the hospital.

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

Following the news of the Crispr babies, researchers sought to prevent more such incidents. Top Chinese bioethicists advocated for a reboot of the country’s medical research regulations .

Hopes and fears around gene editing While the CRISPR baby scandal tarnished the technology’s reputation, CRISPR-Cas9 and related techniques have made a major impact on biomedical research, and ...

CRISPR, the gene-editing technique that can alter any cell and life-form on the planet, exemplifies the point. It can be deployed to alter a bird flu virus to kill multitudes. It can be used for ...

In KJ’s case, CRISPR was moved from the lab into his own body. The work built on research Musunuru has been conducting to fix a genetic mutation in the PCSK9 gene responsible for increasing LDL ...

Personalized CRISPR treatment used on baby with genetic disease by Steph Whiteside - 05/15/25 4:15 PM ET. by Steph Whiteside - 05/15/25 4:15 PM ET.

Bring up germline editing, and most scientists cringe. The idea behind the notorious CRISPR-baby scandal, editing reproductive cells or embryos tinkers with DNA far beyond just the patient—any changes ...

CRISPR Babies: Six years later. Speakers: He Jiankui, CRISPR Pioneer, Antonio Regalado, senior editor for biomedicine, and Mat Honan, editor in chief Gene editing can correct or improve the DNA of ...

National Human Genome Research Institute, accessed Feb. 19, CRISPR Thank you for supporting our journalism. You can subscribe to our print edition, ad-free app or e-newspaper here .

In the latest case, the scientists developed a CRISPR treatment for a boy named KJ, who was born with genetic mutations in his liver cells that prevent him from breaking down proteins properly.

Babies born with CPS1 deficiency can receive liver transplants, but not until they are a year old, long enough that many have already suffered irreversible brain damage. Getting treatment to KJ ...