Neurogene (NASDAQ:NGNE) is advancing a genetic medicines pipeline focused on rare neurologic diseases, with its lead program NGN-401 aimed at treating Rett syndrome, President and CFO Christine Mikail ...

An expert discusses the current treatment landscape of Rett syndrome including the goals of treatment and implications for utilization management strategies with the disease. David Lieberman, MD, PhD: ...

Rett syndrome, a rare and severe neurodevelopmental disorder, affects approximately 1 in 10,000 to 1 in 15,000 live bi ...

Rare genetic disorder shuts off motor skills; mental acuity may still be there. May 9, 2012— -- For the first year of life, Chelsea Coenraads was a perfectly normal child, playing peek-a-boo and ...

Paige Nues provides her closing thoughts regarding the treatment management of Rett syndrome. Paige Nues: We have never felt more optimistic than [at] any time in the Rett syndrome’s history in terms ...

A new UC Davis MIND Institute study offers critical insights into Rett syndrome, a rare genetic condition that affects mostly girls. The research reveals how this condition affects males and females ...

What is Rett syndrome and why does it affect only girls? Rett syndrome is a rare neurological disorder that causes victims to regress intellectually, gradually robbing their ability to think and move.

A University of Virginia School of Medicine scientist is developing an innovative gene therapy she hopes will slow disease progression and improve movement, coordination and communication in children ...

In commemoration of Rett syndrome awareness month this October, Acadia Pharmaceuticals is launching an awareness campaign to shine a light on patients' journeys and show that each person living with ...

AURORA — Recently, NBC correspondent Richard Engel announced his son has a form of Rett Syndrome. It was a shock to everyone especially considering Rett primarily affects girls. I found out Colorado ...

BENGALURU: Awareness about rare diseases can sometimes prevent serious conditions from being overlooked. One such condition is Rett Syndrome, a rare neurological disorder that many people aren’t ...

Acadia Pharmaceuticals (NasdaqGS:ACAD) received a negative trend vote from the European Medicines Agency's Committee for Medicinal Products for Human Use on its Rett syndrome treatment, trofinetide.