A cutting-edge procedure for treating sickle cell disease is changing lives in the St. Louis area, where an estimated 1,200 ...

CHANGING THE LIVES OF SICKLE CELL DISEASE PATIENTS. ONE LOCAL MAN IS FINALLY GETTING RELIEF FROM THE CRIPPLING PAIN HE’S EXPERIENCED FOR YEARS. OUR JESSICA BROWN IS HERE WITH HIS STORY. PATIENTS TELL ...

Doctors say new gene-based treatments could offer long-term relief — and possible cures — for people living with sickle cell disease. Sickle cell disease has long shortened lives in the United States, ...

More quality-adjusted life-years with gene therapy, but at a much higher cost ...

A new gene therapy at Barnes-Jewish Hospital in St. Louis may cure a man whose life has been defined by sickle cell disease.

Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment opportunity for sickle cell disease and β-thalassemia. The discovery, ...

Treatment with exagamglogene autotemcel (exa-cel) led to robust and sustained improvements in quality of life for patients with severe sickle cell disease (SCD) or transfusion-dependent beta ...

Millions of Americans have seen their health insurance premiums skyrocket since the Affordable Care Act subsidies expired at the end of December. Congress has worked to try and extend the COVID-19 era ...

The first patient in Louisiana to receive genetically edited therapy for sickle cell disease went home this week after months in isolation at Manning Family Children's Hospital in New Orleans. Daniel ...

The Scottish Medicines Consortium (SMC) has accepted exagamglogene autotemcel (Casgevy, Vertex Pharmaceuticals) for use within NHS Scotland to treat sickle cell disease (SCD) in patients aged 12 years ...

Stem cell transplantation is the most cost-effective option for long-term care of sickle cell disease in adults when compared with gene therapy and standard of care treatment, according to new ...