Children with sickle cell anemia show subtle brain changes in certain regions, even without prior stroke or infarction, a new ...

After a meeting with the FDA, Agios Pharmaceuticals is planning to seek accelerated approval in the U.S. of mitapivat for ...

An application to the U.S. Food and Drug Administration is expected to be supported by data that showed risto-cel's benefit ...

Dunstan Nicol-Wilson is a clinical project manager from South East London, United Kingdom. Dunstan has his master’s in public health with a global health focus. Dunstan was diagnosed with the ...

A Japan national funding agency has awarded $32 million to advance EPF-001, a treatment for sickle cell disease, into ...

As the season shifts from winter to spring, I’ve found myself reflecting deeply on what this past winter has meant for me. I’m incredibly grateful, and I know it didn’t happen by chance. It was the ...

FTX-6058 is an experimental small molecule treatment for sickle cell disease (SCD) being developed by Fulcrum Therapeutics. It aims to treat patients by raising levels of fetal hemoglobin in cells.

A Nigerian hematologist will pursue a PhD in health policy at the University of Tennessee Health Science Center to help advance her work on programs for sickle cell disease (SCD) in her home country.

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Top-line data revealed olinciguat was well-tolerated across all doses tested, but the therapy’s ...

Children’s Hospital Los Angeles (CHLA) is now offering Casgevy (exagamglogene autotemcel), an approved gene-editing therapy for sickle cell disease (SCD). “This is a transformative time for Children’s ...

Sickle cell disease (SCD) may be cured in some individuals by a stem cell transplant. There also are several approved therapies to help manage the condition and its related complications. Some of the ...

A $1.9-million federal grant has been awarded to a clinical trial that seeks to find effective ways to improve adherence to hydroxyurea treatment among children and young adults with sickle cell ...