Scholar Rock Application for Spinal Muscular Atrophy Treatment Gets FDA Approval
Apitegromab is an investigational treatment aimed at improving motor function for people living with spinal muscular atrophy. Scholar Rock said it has also submitted and received validation for its ...
BioSpace2d
6 Therapies on the Horizon for Spinal Muscular Atrophy
Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...
The Brighterside of News on MSN5d
Neanderthals were smarter, stronger, and more human than previously known
More than a century ago, a distorted image of Neanderthals emerged. When a nearly complete skeleton was discovered in 1908 at La Chapelle-aux-Saints, France, its reconstruction led to lasting ...
The Boeing Starliner Saga left Sunita Williams struggling—But now comes her toughest mission yet
After a grueling nine-month mission aboard the International Space Station, astronaut Sunita Williams returned to Earth ...
SMA News Today6d
MDA 2025: SMA kids maintaining Zolgensma benefits 10 years later
Children with SMA given the gene therapy Zolgensma in infancy are maintaining motor milestones after up to 10 years, new ...
STAT6d
Novartis finally delivers gene therapy data in older SMA patients. Will they still want it?
In the time since the Novartis gene therapy Zolgensma was approved for babies with spinal muscular atrophy, other treatments ...