Apitegromab is an investigational treatment aimed at improving motor function for people living with spinal muscular atrophy. Scholar Rock said it has also submitted and received validation for its ...
Since 2016, the FDA has approved three disease-modifying treatments for spinal muscular atrophy, with several ...
More than a century ago, a distorted image of Neanderthals emerged. When a nearly complete skeleton was discovered in 1908 at La Chapelle-aux-Saints, France, its reconstruction led to lasting ...
After a grueling nine-month mission aboard the International Space Station, astronaut Sunita Williams returned to Earth ...
Children with SMA given the gene therapy Zolgensma in infancy are maintaining motor milestones after up to 10 years, new ...
In the time since the Novartis gene therapy Zolgensma was approved for babies with spinal muscular atrophy, other treatments ...
Learning from examples like congenital heart disease and cystic fibrosis can help health systems and clinicians prepare to care for an influx of patients with neuromuscular diseases as they reach ...
NASA’s Crew-10 mission will bring back Butch Wilmore and Sunita Williams after nine months on the ISS. Their extended stay ...
Arthritis is a common condition that causes pain and inflammation in the joints. If you're looking to manage symptoms of the ...
Therefore, option (c) is the correct answer. — A two-and-a-half-year-old girl has shown no signs of a genetic disorder — known as spinal muscular atrophy (SMA) — becoming the first person in the world ...
Hi friends! Shane here! I just wanted to quick put up some reflections on my day today. I got my 7th Spinraza injection and it was quite a long day! 'America is not Canada,' new Prime Minister ...